Advances In Gene Editing Technologies For Disease Treatment: Potential And Challenges

Authors

  • Dr. Ayesha Raza Department of Molecular Medicine, Aga Khan University, Karachi, Pakistan. Author

Keywords:

Gene editing, CRISPR, genetic disorders, disease treatment, base editing, prime editing, personalized medicine

Abstract

Gene editing technologies, particularly CRISPR-Cas9, have revolutionized the field of genetics and opened new possibilities for the treatment of genetic disorders. These technologies allow for precise modification of DNA sequences, providing potential cures for diseases that were previously considered untreatable. This article explores the advances in gene editing technologies and their applications in disease treatment, focusing on the role of CRISPR-Cas9, base editing, and prime editing. It examines the therapeutic potential of these technologies in treating a wide range of genetic disorders, including inherited diseases, cancer, and viral infections. Additionally, the article discusses the ethical considerations, regulatory challenges, and potential risks associated with gene editing. Case studies from the United States, Argentina, Pakistan, and South Africa are presented to illustrate the current state of gene editing research and clinical applications. The article concludes with a discussion of the future directions for gene editing technologies and their role in personalized medicine.

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Published

2025-06-30